Genetic therapy for EYS- and USH2A-associated retinal disease
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Titel: USH2A variants causing retinitis pigmentosa or Usher syndrome provoke differential retinal phenotypes in disease-specific organoids.
Auteur: Sanjurjo-Sanjurjo C, Jimenez-Medina C, Erkilic N, Cappellino L, Lefevre A, Nagel-Wolfrum K, Wolfrum U, Van Wijk E, Roux A-F, Meunier I and Kalatzis V
Magazine: HGG Advances
Begin- en eindpagina: 100229-100229
Link: https://pubmed.ncbi.nlm.nih.gov/37654703/
Auteur: Sanjurjo-Sanjurjo C, Jimenez-Medina C, Erkilic N, Cappellino L, Lefevre A, Nagel-Wolfrum K, Wolfrum U, Van Wijk E, Roux A-F, Meunier I and Kalatzis V
Magazine: HGG Advances
Begin- en eindpagina: 100229-100229
Link: https://pubmed.ncbi.nlm.nih.gov/37654703/